Octagenix

Rare Diseases

Rare Diseases

Vaccine Supply for Healthcare Systems Worldwide

Product Overview

Rare diseases often present some of the most challenging sourcing requirements in healthcare, particularly when products are approved in limited markets or needed for small patient populations. OctaGenix has the capability to support the procurement of premium products for rare and ultra-rare conditions, helping bridge access gaps for healthcare providers and specialist centres.

Human Vaccine Categories We Can Support

As orphan drugs are usually very expensive, OctaGenix uses its global sourcing channels to identify and procure products at more affordable prices for healthcare systems, while maintaining a strong focus on quality, authenticity, and compliance. By improving cost-effective access to rare disease treatments, OctaGenix helps enhance patient access to essential therapies that may otherwise be difficult to obtain due to limited availability, high cost, or complex supply routes.

Get in Contact?

Get in touch with our team to discuss product availability, procurement requirements, and how OctaGenix can support your healthcare supply needs.

ProductStrengthFormulation
Bleomycin (Lyophilized)15 IURare oncology / hematologic malignancy
Cytarabine100mg/ml; 500mg/5ml; 1000mg/10mlRare oncology / hematologic malignancy
Dactinomycin (Lyophilized)500mcgRare oncology / pediatric solid tumor
Daunorubicin (Lyophilized)20mgRare oncology / hematologic malignancy
Fludarabine50mg/2mlRare oncology / hematologic malignancy
L-Asparaginase (Lyophilized)5000 IU; 10000 IURare oncology / acute lymphoblastic leukemia
Leuprolide3.75mg; 7.5mg; 11.25mg; 22.5mgRare endocrine / central precocious puberty
Pemetrexed (Lyophilized)100mg; 500mgRare oncology / mesothelioma
Temoporfin1mg/mlRare oncology / photodynamic therapy
Vincristine1mg/ml; 2mg/2mlRare oncology / hematologic or pediatric cancer
Pamidronate / Di-Sodium Pamidronate (Lyophilized)30mg; 60mg; 90mgRare bone disease / osteogenesis imperfecta use
Zoledronic Acid (Lyophilized)4mgRare bone disease / osteogenesis imperfecta use
Desmopressin4mcg/mlRare endocrine / central diabetes insipidus
Somatropin (HGH)4 IU; 10 IU; 12 IU; 16 IU; 24 IURare endocrine / genetic growth disorder
Octreotide50mcg; 100mcg; 200mcgRare endocrine / acromegaly or neuroendocrine tumor
Erythropoietin(2000; 3000; 4000; 5000; 10000; 20000; 40000) IU/mlRare hematology / anemia syndromes
Filgrastim300mcg/1mlRare hematology / severe congenital neutropenia
Azacitidine Injection (Lyophilized)100 mgRare oncology / myelodysplastic syndromes
Bortezomib Injection2mg; 3.5mgRare oncology / multiple myeloma
Desferrioxamine Injection500 mgRare hematology / transfusional iron overload
Interferon Beta Injection30mcgRare neurologic / demyelinating disease
Melphalan Injection50 mgRare oncology / multiple myeloma
Pegaspargase Injection3,750 IURare oncology / acute lymphoblastic leukemia
Thiotepa Injection (Lyophilized)15mg; 100 mgRare oncology / transplant conditioning or rare cancers
Tocilizumab Injection200 mg/10 mlRare inflammatory / Castleman disease or systemic JIA
Chlorambucil20mgRare oncology / hematologic malignancy
Fludarabine Phosphate10mgRare oncology / hematologic malignancy
Imatinib100mg; 400mgRare oncology / CML or GIST
Tretinoin10mg; 20mgRare oncology / acute promyelocytic leukemia
Alfacalcidol0.25mcg; 0.5mcg; 1mcgRare endocrine / hypoparathyroidism-related use
Deflazacort1mg; 6mg; 12mg; 18mg; 30mgRare genetic neuromuscular disease / Duchenne muscular dystrophy
Acitretin10mg; 25mgRare dermatology / disorders of keratinization
Deferiprone250mgRare hematology / transfusional iron overload
Nilotinib200mgRare oncology / CML
Crizotinib250mgRare oncology / ALK-positive tumors
Etoposide50mg; 100mgRare oncology / hematologic or germ-cell malignancy
Hydroxyurea250mg; 500mgRare hematology / sickle cell disease or myeloproliferative neoplasm
Imatinib Mesylate100mg; 400mgRare oncology / CML or GIST
Lenalidomide10mg; 15mgRare oncology / multiple myeloma or MDS
Lenvatinib10 mgRare oncology / thyroid cancer
Procarbazine50mgRare oncology / Hodgkin lymphoma or brain tumors
Sunitinib12.5mg; 25mg; 37.5mg; 50mgRare oncology / GIST or pancreatic NET
Temozolomide20mg; 100mg; 250mgRare oncology / glioma
Thalidomide50mg; 100mg; 150mg; 200mg; 300mgRare oncology / multiple myeloma; rare inflammatory use